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P Harmatz Selected Research

P Harmatz Research Topics

Disease

5Mucopolysaccharidosis VI (Syndrome, Maroteaux-Lamy)
01/2017 - 03/2004
2Mucopolysaccharidosis II (Hunter Syndrome)
09/2017 - 12/2009
2Lysosomal Storage Diseases (Lysosomal Storage Disease)
05/2012 - 03/2005
1Mucopolysaccharidoses
01/2017
1Disease Progression
01/2017
1Mucopolysaccharidosis IV (Morquio Syndrome)
09/2013
1Multiple Sulfatase Deficiency Disease (Mucosulfatidosis)
05/2012
1Fibrosis (Cirrhosis)
07/2000
1Sickle Cell Anemia (Hemoglobin S Disease)
07/2000
1Iron Overload
07/2000

Drug/Important Bio-Agent (IBA)

4EnzymesIBA
09/2013 - 03/2005
3GlycosaminoglycansIBA
09/2017 - 12/2009
3N-Acetylgalactosamine-4-Sulfatase (Arylsulfatase B)IBA
01/2017 - 03/2004
2galsulfaseFDA Link
01/2017 - 03/2013
2SulfatasesIBA
09/2013 - 05/2012
1AntibodiesIBA
09/2017
1idursulfaseFDA Link
09/2017
1CreatinineIBA
01/2017
1Dermatan SulfateIBA
01/2017
1AcetylgalactosamineIBA
03/2005
1IronIBA
07/2000
1Ferritins (Ferritin)IBA
07/2000

Therapy/Procedure

6Enzyme Replacement Therapy
09/2017 - 03/2004
3Therapeutics
03/2013 - 07/2000
1Chelation Therapy (Therapy, Chelation)
07/2000
1Erythrocyte Transfusion
07/2000